Asthma and Nontuberculous Mycobacterial (NTM) Lung DiseaseAn estimated 86,000 people in the United States live with nontuberculous mycobacterial (NTM) lung disease. And the number of people diagnosed with NTM – especially among women and older adults...reactionscomments
Community Spotlight: Glycogen Storage DiseasesGlucose is an important sugar that bodies need for energy. The body packs small molecules of glucose into large molecules called glycogen. Glycogen is stored in the cells of the...reactionscomments
Community Spotlight: Rare CancersRare cancers affect fewer than 40,000 people per year in the United States. These cancers make up about a quarter of all cancers and account for about a quarter of...reactionscomments
What Is Gene Therapy?Genes are the pieces of DNA that make us who we are. They determine our eye and hair color, how tall we will be, and if we are prone to...reactionscomments
ICD Codes: Why They Matter in Rare DiseaseThe International Statistical Classification of Diseases and Related Health Problems (ICD) is used worldwide to standardize the classification of diseases. It is used as a uniform way to collect statistics...reactionscomments
Genetics 101Our genes are like a recipe book for our bodies. They tell our cells what to do, how to grow, and how to repair themselves. Genes play a role in...reactionscomments
Understanding Clinical TrialsA clinical trial is a type of research. Research is the process scientists use to explain how our bodies work or why our bodies stop working well. Clinical trials are...reactionscomments
Clinical Trial GlossaryClinical trials or studies have a language of their own. It helps to understand the common terms doctors use when talking about a clinical trial before you sign up. Here...reactionscomments
Clinical Trial ParticipationClinical trials are medical studies that pose a question: Does a new treatment work better than older treatments? Each year, thousands of treatments are tested in controlled experiments called clinical...reactionscomments
